Buscar resultados de ensayos clínicos
Metachromatic Leukodystrophy - 25 Studies Found
Estado | Estudiar |
Active, not recruiting |
Nombre del estudio: The Natural History of Metachromatic Leukodystrophy Condición: Metachromatic Leukodystrophy Fecha: 2008-03-11 |
Completed |
Nombre del estudio: Multicenter Study of HGT-1110 Administered Intrathecally in Children With Metachromatic Leukodystrophy (MLD) Condición: Metachromatic Leukodystrophy (MLD) Fecha: 2011-12-14 Intervenciones: Biological: Recombinant human arylsulfatase A 6 patients treated with HGT-1110 EOW by IT injection |
Completed |
Nombre del estudio: Effect of Warfarin in the Treatment of Metachromatic Leukodystrophy Condición: Metachromatic Leukodystrophy Fecha: 2008-05-21 Intervenciones: Drug: Warfarin Oral administration (QD), variable dosage: patients will undergo blood test for PT/INR at |
Completed |
Nombre del estudio: Efficacy METAZYM for the Treatment Metachromatic Leukodystrophy Treated With Hematopoietic Stem Cell Transplantation Condición: Metachromatic Leukodystrophy Fecha: 2011-02-23 Intervenciones: Drug: rhARSA intravenous infusion 100U/kg every other week for 18 months |
Recruiting |
Nombre del estudio: Intracerebral Gene Therapy for Children With Early Onset Forms of Metachromatic Leukodystrophy Condición: Metachromatic Leukodystrophy Fecha: 2013-01-28 Intervenciones: Genetic: intracerebral administration of AAVrh.10cuARSA |
Completed |
Nombre del estudio: Long-term Metazym Treatment of Patients With Late Infantile Metachromatic Leukodystrophy (MLD) Condición: Late Infantile Metachromatic Leukodystrophy Fecha: 2008-02-29 Intervenciones: Biological: Recombinant human Arylsulfatase A (rhASA) intravenous infusion, every other week for 26 week |
Completed |
Nombre del estudio: Imaging Study of the White Matter Lesions in Children With Metachromatic Leucodystrophy Condición: Late Infantile Metachromatic Leukodystrophy Fecha: 2011-03-09 Intervenciones: Other: High-field MRI (3 Teslas) |
Terminated |
Nombre del estudio: Open-Label Extension Study of Recombinant Human Arylsulfatase A (HGT-1111) in Late Infantile MLD Condición: Late Infantile Metachromatic Leukodystrophy Fecha: 2008-05-19 Intervenciones: Drug: HGT-1111 Patients currently dosed with 100 U/kg or 200 U/kg will continue this treatment. Patients |
Enrolling by invitation |
Nombre del estudio: Open-Label Extension Study Evaluating Safety and Efficacy of HGT-1110 in Patients With Metachromatic Leukodystrophy Condición: Metachromatic Leukodystrophy (MLD) Fecha: 2013-06-20 Intervenciones:
|
Completed |
Nombre del estudio: Metazym for the Treatment of Patients With Late Infantile Metachromatic Leukodystrophy (MLD) Condición: Metachromatic Leukodystrophy (MLD) Fecha: 2007-01-04 Intervenciones: Drug: rhASA intravenous infusion 25 U/kg,50 U/kg, 100U/kg or 200 U/kg every other week for 26 weeks |